Antisense, gene therapy, and stem cell news, and the Blues Brothers
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"I want four fried chickens and a Coke".  Dr. Charis Himeda joins us as we discuss some encouraging recent data from Sarepta for one of their DMD gene therapy trials and from Avidity for their myotonic dystrophy phase I/II trial and how it all potentially impacts FSHD.  In addition, we revisit the potential (or lack there of) for placental or umbilical cord derived stem cell therapy for FSHD. --- Send in a voice message: https://anchor.fm/peter-l-jones/message
More Episodes
"Whatchyou talkin' 'bout Willis?" In a field where every press release is met with unsubstantiated hoopla and proclamations of BREAKTHROUGH! to fire you up to shake you down, we finally have some real news. We provide our evaluation of Avidity's public interim report on their FORTITUDE AOC-1020...
Published 06/14/24
Published 06/14/24
"You're messing with the wrong guy!!!!" We expand a bit more on the utility of the FSHD-like pig model and then discuss the science behind and implications of p38 inhibition for FSHD. --- Send in a voice message: https://podcasters.spotify.com/pod/show/peter-l-jones/message
Published 06/01/24