When patients face the diagnosis of a rare disease, they face a costly, uphill battle to develop a treatment for their condition… that is, if they ever do.     Dr. Stanley Crooke is aiming to change that. As the CEO of n-Lorem Foundation, his mission is to provide personalized treatments to ultra-rare disease patients for free as long as they live, no questions asked. Thanks to his humility, coupled with the generosity of other individuals and companies, ultra-rare disease patients have a renewed hope to get the treatments others may not be able to provide.     Join Dr. Crooke as he reflects on his humble beginnings at Ionis, the approach n-Lorem takes to developing drugs for ultra-rare diseases, and what the future holds for research in this area. Show Notes  n-lorem Foundation  Charles River - Rare Disease  Vital Science S4, E01 Project ALS: Fueled by Love  2021 Rare Disease Trailblazers  BioSpace: n-Lorem Foundation Preps First Doses to Treat Ultra-Rate Disease Patients for Free  Ionis Pharmaceuticals  Nature Medicine: Antisense oligonucleotide silencing of FUS expression as a therapeutic approach in amyotrophic lateral sclerosis